Stuart W Peltz Selected Research

ataluren

12/2021	Meta-analyses of deflazacort versus prednisone/prednisolone in patients with nonsense mutation Duchenne muscular dystrophy.
10/2020	Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy.
11/2018	Deflazacort versus prednisone/prednisolone for maintaining motor function and delaying loss of ambulation: A post HOC analysis from the ACT DMD trial.
1/2017	Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial.
10/2014	Ataluren treatment of patients with nonsense mutation dystrophinopathy.
7/2014	Ataluren for the treatment of nonsense-mutation cystic fibrosis: a randomised, double-blind, placebo-controlled phase 3 trial.
1/2013	Phase 2a study of ataluren-mediated dystrophin production in patients with nonsense mutation Duchenne muscular dystrophy.
1/2013	Ataluren as an agent for therapeutic nonsense suppression.
2/2008	PTC124 is an orally bioavailable compound that promotes suppression of the human CFTR-G542X nonsense allele in a CF mouse model.
5/2007	PTC124 targets genetic disorders caused by nonsense mutations.

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Stuart W Peltz Research Topics

Disease

9	Duchenne Muscular Dystrophy (Muscular Dystrophy, Becker) 12/2021 - 04/2007
7	Inborn Genetic Diseases (Disease, Hereditary) 01/2017 - 04/2007
4	Neoplasms (Cancer) 01/2019 - 01/2016
3	Cystic Fibrosis (Mucoviscidosis) 07/2014 - 04/2007
3	Infections 07/2013 - 02/2003
2	Disease Progression 10/2020 - 01/2020
2	Hypoxia (Hypoxemia) 07/2016 - 01/2016
1	Neurodegenerative Diseases (Neurodegenerative Disease) 12/2021
1	Huntington Disease (Huntington's Disease) 12/2021
1	Inflammation (Inflammations) 01/2021
1	COVID-19 01/2021
1	Leukemia 01/2019
1	Hematologic Neoplasms (Hematological Malignancy) 01/2019
1	Ovarian Neoplasms (Ovarian Cancer) 01/2017
1	Virus Diseases (Viral Diseases) 07/2016
1	Muscular Diseases (Myopathy) 10/2014
1	Acute Kidney Injury (Acute Renal Failure) 07/2014
1	Chronic Hepatitis C 07/2013
1	type 2B Limb-girdle muscular dystrophy 09/2010
1	Miyoshi myopathy 09/2010
1	Dizziness (Lightheadedness) 04/2007
1	Headache (Headaches) 04/2007
1	Breast Neoplasms (Breast Cancer) 04/2006

Drug/Important Bio-Agent (IBA)

14	Nonsense Codon (Nonsense Mutation)IBA 12/2021 - 04/2007
11	atalurenIBA 12/2021 - 04/2007
7	Pharmaceutical PreparationsIBA 01/2019 - 02/2003
5	Proteins (Proteins, Gene)FDA Link 01/2016 - 05/2007
4	Messenger RNA (mRNA)IBA 01/2016 - 04/2006
3	emvododstatIBA 01/2021 - 07/2016
2	Prednisone (Sone)FDA LinkGeneric 12/2021 - 01/2020
2	Prednisolone (Predate)FDA LinkGeneric 12/2021 - 01/2020
2	deflazacortIBA 12/2021 - 01/2020
2	CytokinesIBA 01/2021 - 01/2016
2	Vascular Endothelial Growth Factor A (Vascular Endothelial Growth Factor)IBA 01/2019 - 01/2016
2	3' Untranslated Regions (3' UTR)IBA 01/2016 - 04/2006
1	CytosineIBA 12/2021
1	Adenine FDA LinkGeneric 12/2021
1	GuanineIBA 12/2021
1	Uracil NucleotidesIBA 01/2019
1	Biological ProductsIBA 01/2019
1	Phosphotransferases (Kinase)IBA 01/2019
1	pyrimidineIBA 01/2019
1	EnzymesIBA 01/2019
1	Dihydroorotate DehydrogenaseIBA 01/2019
1	NucleotidesIBA 01/2019
1	clitocineIBA 01/2017
1	Investigational DrugsIBA 10/2014
1	Tobramycin (Nebcin)FDA LinkGeneric 07/2014
1	CreatinineIBA 07/2014
1	ChloridesIBA 07/2014
1	Antiviral Agents (Antivirals)IBA 07/2013
1	6- (3- cyano- 6- ethyl- 5- fluoro- 1- (pyrimidin- 2- yl)- 1H- indol- 2- yl)- N- (1,1,1- trifluoropropan- 2- yl)pyridine- 3- sulfonamideIBA 07/2013
1	DystrophinIBA 01/2013
1	DysferlinIBA 09/2010
1	Terminator Codon (Termination Codon)IBA 02/2008
1	SuspensionsIBA 04/2007

Therapy/Procedure

4	Therapeutics 01/2021 - 07/2013
1	Oral Administration 01/2016
1	Highly Active Antiretroviral Therapy (HAART) 02/2003